Status | Study |
Recruiting |
Study Name: Analysis of Patients Treated for Chronic Granulomatous Disease Since January 1, 1995 Condition: Chronic Granulomatous Disease Date: 2014-04-15 |
Recruiting |
Study Name: Patients Treated for Chronic Granulomatous Disease (CGD) Since 1995 Condition: Granulomatous Disease, Chronic Date: 2014-03-06 |
Recruiting |
Study Name: Gene Therapy for X-linked Chronic Granulomatous Disease (X-CGD) Condition: X-Linked Chronic Granulomatous Disease Date: 2013-05-14 Interventions: Genetic: X vivo gene therapy Transplantation of patient's autologous CD34+ cells transduced with lentivi |
Recruiting |
Study Name: Radiofrequency Ablation for Liver Abscesses From Chronic Granulomatous Disease Condition: Chronic Granulomatous Disease (CGD) Date: 2013-05-08 Interventions: Device: Cool-tip RF Ablation System RFA therapy will be administered according to the instructions of th |
Withdrawn |
Study Name: Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease (X-CGD) Condition: Granulomatous Disease, Chronic, X-linked, Variant Date: 2011-06-23 Interventions: Genetic: pCCLchimGp91s lentiviral vector transduced CD34+ cells infusion pCCLchimGp91s lentiviral vector |
Recruiting |
Study Name: Targeted Busulfan, Fludarabine Conditioning Regimen for Hematopoietic Stem Cell Transplantation in Chronic Granulomatous Disease(CGD) Condition: Chronic Granulomatous Disease Date: 2011-03-04 Interventions: Drug: Busulfan First dose: busulfan (120 mg/m2 ivs once daily) (if age<1 yr: 80 mg/ m2) Second to for |
Completed |
Study Name: Gene Therapy for X-linked Chronic Granulomatous Disease (CGD) in Children Condition: Chronic Granulomatous Disease Date: 2009-06-22 Interventions: Genetic: retroviral SF71-gp91phox transduced CD34+ cells autologous ex-vivo transduced (SF71-gp91phox)CD |
Completed |
Study Name: Pharmacokinetics of Posaconazole in Children With Chronic Granulomatous Disease (CGD) Condition: Chronic Granulomatous Disease Date: 2008-11-26 Interventions: Drug: posaconazole (PSZ) Intake of PSZ oral suspension 40mg/ml twice daily with food. Starting dose is b |
Active, not recruiting |
Study Name: Gene Therapy for Chronic Granulomatous Disease in Korea Condition: Chronic Granulomatous Disease Date: 2008-10-21 Interventions: Drug: VM106 Autologous hematopoietic stem cells with MT-gp91 retroviral vector |
Recruiting |
Study Name: Matched Unrelated or Non-Genotype Identical Related Donor Transplantation For Chronic Granulomatous Disease Condition: Chronic Granulomatous Disease Date: 2007-12-19 Interventions: Drug: Busulfan |